These stories are shared for educational purposes only and are not intended to discuss or imply any information about investigational therapies not approved by the FDA and where safety and efficacy have not been established. Any questions regarding a medical condition, treatment, or decisions regarding whether to participate in a clinical trial should always be directed to a healthcare professional. Each person’s individual results and situation will vary.
Patient Community Stories
Patients are why we’re here—these are a few of their stories.
Huntington’s Disease
Hemophilia B
