uniQure’s sole purpose is to help patients and the people who care for them.
We hope to be a resource for patients about how gene therapy may help.

uniQure is working on delivering on the promise of gene therapy, single treatments with potentially curative results. In our commitment to rapidly bring new disease modifying  therapies to patients with severe genetic diseases, we are collaborating with Patient Advocacy organizations listed at our community resources page.

We are also committed to keeping you informed on our latest developments, for which you can sign-up here.

Edwin, a participant in the Phase 1-2 clinical trial of AMT-060

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• > Huntington's Disease
• > Congestive Heart Failure
• > LPLD
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